Emil Kakkis
President and CEO,
Ultragenyx
United States
Dr. Emil Kakkis is Chief Executive Officer, President and Founder of Ultragenyx, a company with four approved therapies for five rare diseases and multiple late-stage clinical programs. He is best known for his work developing novel treatments for rare diseases and working on policy issues affecting rare and ultrarare disease treatment. Dr. Kakkis has received numerous awards including the Life Science Leadership Pantheon award from California Life Sciences, a Lifetime Achievement Award from the National MPS Society, the Roscoe O. Brady Award for innovation from the WORLDSymposium and BIO’s Henri Termeer Visionary Leadership award for his transformative work in rare diseases.
Sessions
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16-Jun-2025206ABLeveraging the Accelerated Approval Pathway for Rare Diseases
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18-Jun-2025254BOptimizing Clinical Trial Design and Execution for Rare Diseases


