
Tracey Sikora
Vice President of Research and Clinical Programs
National Organization for Rare Disorders (NORD)
Tracey Sikora is Vice President of Research and Clinical Programs at the National Organization for Rare Disorders (NORD). She has a 15+ year career conducting pre-clinical and clinical research in multiple rare diseases, including MPS I, VI, and VII, Duchenne Muscular Dystrophy, Krabbe disease, Niemann-Pick Type C, Familial Hypercholesterolemia, and Castleman disease. Her research portfolio at the University of Pennsylvania included novel treatments such as lentiviral vector and AAV-based gene therapies and repurposed treatments such as miglustat. In 2022, Tracey co-founded Every Cure, a nonprofit biotech organization dedicated to finding additional uses for existing drugs using novel technical approaches and artificial intelligence.
Speaking In
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17-Jun-2025