Lessons from the Oregon Trail: Pioneering Gene Therapy in the Real World
Monday, June 03, 2024
Breakout Session
![Cell and Gene Therapy and Genome Editing](https://cdn.asp.events/CLIENT_BIO_7BB99CBA_BAD1_B8C8_CF9F25DA29A80CC6/sites/BIOIC-2024/media/icons/seminars/BIO-track-icon_GeneEditing_MTC.png)
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Gene therapies hold the potential to transform – and even cure – severe genetic diseases and offer new hope for patients and families. Yet moving these promising results from the confines of a clinical trial setting into the “real world” is not for the faint of heart. Delivering one-time therapies – as opposed to chronic, lifelong treatments – requires a different approach from manufacturers, CDMOs, health systems, payers, and patients, and overcoming these challenges is essential for the field to deliver on its long-awaited promise to patients.
Hear firsthand from pioneers who've played pivotal roles in delivering the first gene therapies to patients in a commercial setting. The discussion will also include patient perspective on the gene therapy treatment journey.
Moderator
Speakers
![](https://www.conferenceharvester.com/uploads/harvester/photos/XDQDGWMO-Presenter-OlsonT.jpg)
Medical Director, Blood and Marrow Transplant Program
Children's Hospital of Philadelphia